Bubble boy disease is the most common SCID condition, and the frequency of the illness isn't known. But researchers are hopeful that the technique could offer a brighter future to families who receive this traumatic diagnosis. The condition affects around one in 200,000 babies, mostly boys, and was brought into the public eye by a boy called David Vetter, who was born in Texas in 1971. While X-SCID is extremely rare, scientists are also using gene therapy to create treatments for other, more common conditions including cancer and blindness. They are also in charge of making antibodies, which are blood proteins that identify toxins that need to be destroyed. A similar technique harnessing a modified version of HIV is also being studied as a possible cure for sickle cell anemia, CBS News chief medical correspondent Dr. Jon LaPook reports. He just kept getting these infections," said his mother, Kristin Simpson. Four were treated at St. Jude’s Children’s Research Hospital, and four were treated at UCSF Benioff Children’s Hospital. However, it’s tough to find a match. "This therapy has cured the patients," although it will take more time to see if it's a permanent fix, said Dr. Ewelina Mamcarz, one of the study leaders at St. Jude Children's Research Hospital in Memphis. This material may not be published, broadcast, rewritten, or redistributed. Thanks to the therapy, Omarion now has a normal immune system. Recently, experts at the Children’s Research Hospital have been able to cure babies born with the Bubble Boy Disease with a new gene therapy, reports a research published the New England Journal of Medicine. "This is the first time we've seen a total reconstruction of the immune system, which has provided the ability for these children to get out of isolation. If the immune function cannot be regained, then kids with this condition live only for one or two years. They can survive if they have a bone marrow transplant, giving them a new immune system – however this can take up to two years and is not successful in all patients. Bubble boy disease refers to one of several genetic disorders that manifest as an inability by the body to produce cells that battle infection or illness. Most of these are blood tests. "To me, this looks promising.". Bubble boy disease is caused by mutations in a gene called IL2RG on the X chromosome. Immunoglobulin levels (IgG, IgM, IgA, IgE) – These are antibodies made by your immune cells to fend off germs. It has been tried on 10 children so far in Tennessee and UCSF Benioff Children's Hospital in San Francisco. You can unsubscribe at any time. 0. "The question will become: Will it be a durable cure? "I would put him to the hospital window so he could see people walk and cars go by. They were also responding to vaccines, observed the research authors. Dr. Mamcarz and her co-authors are very optimistic about the trail's results. He's now able to go outdoors. SCID-X1, often referred to as Bubble Boy Disease, owes this name to Vetter. But I haven't heard of a kid in a bubble in a long time. Other manifestations to watch out for include recurrent diarrhoea and severe rashes. The most common type is linked to the X-chromosome, making this form affect only males. This is typically a hereditary disorder that can be passed on by a mother or father, in whom the disorder is recessive and so some offspring may not have the disease while others do. David could only have been cured by a bone marrow transplant but he died shortly after having one, when he was just 12 years old. For example, David, pictured above, had to live in this plastic "bubble" while doctors searched for a cure for his condition.

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